Dame Margaret Brimble: Professor on the brink of history with breakthrough treatment for Rett Syndrome

Published: March 9, 2023, 6:50 p.m.

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A New Zealand chemist is on the brink of history, with her breakthrough treatment for Rett Syndrome.

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Distinguished Professor Dame Margaret Brimble and her team has been working on the drug for 20 years.

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They expect to hear within days whether their treatment Trofinetide has been granted final approval by the US Food and Drug Administration.

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Brimble told Mike Hosking it\'ll be a life changer for babies born with the syndrome.

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The disorder impacts almost exclusively females, and stalls motor control and communications in infants.

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